hrp0098p1-265 | Growth and Syndromes 4 | ESPE2024

Use of Vosoritide in Children with Achondroplasia - Real Life Experince

Kahveci Ahmet , Helvacıoglu Didem , Yavas Abalı Zehra , Tugba Canbaz Aylin , Gunay Aylin , Bereket Abdullah , Demircioglu Turan Serap

Aim and Method: Achondroplasia is the most common form of short-limbed dwarfism, characterized by mutations in the FGFR3 gene. Vosoritide, a C-type natriuretic peptide analog, has shown promise in promoting linear growth in children with achondroplasia. This study aims to present the real-life experiences of using vosoritide in children diagnosed with achondroplasia.Method and Results: A prospective study was conducted o...