Higher Dose of Burosumab is Needed for Treatment of Children with Severe Forms of X-Linked Hypophosphatemia
1APHP, Reference Center for Rare Disorders of the Calcium and Phosphate Metabolism, Filiere OSCAR and Platform of expertise for rare diseases Paris-Sud, Bicêtre Paris-Sud Hospital, Le Kremlin-Bicetre, France. 2Department of Clinical Medicine and Surgery, Division of Endocrinology, University of Naples Federico II, Naples, Italy. 3APHP, Department of Endocrinology and Diabetology for children, Bicêtre Paris-Sud Hospital, Le Kremlin-Bicetre, France. 4APHP, Department of Endocrinology and Reproductive Diseases, Bicêtre Paris-Sud Hospital, Le Kremlin-Bicetre, France. 5Paris Sud Paris Saclay University, Faculté de Médecine, Le Kremlin-Bicetre, France. 6APHP, Department Pediatric Radiology, Bicêtre Paris-Sud Hospital, Le Kremlin-Bicetre, France. 7APHP, Department of ORL, Bicêtre Paris-Sud Hospital, Le Kremlin-Bicetre, France. 8APHP, Department of Odontology-Maladies Rares, Hospital Bretonneau Paris, Paris, France. 9Université Paris Descartes Paris, Paris, France. 10APHP, Department of Pediatric orthopaedic surgery, Necker - Sick Kids University Hospital, Paris, France. 11APHP, Department of Rheumatology Hospital Cochin, Paris, France. 12Pediatric Neurosurgery, Hospital Femme Mere Enfant, Hospices Civiles de Lyon and University Claude Bernard Lyon, Bron Cedex, France. 13Reference Center for Craniosynostosis, INSERM 1033, Lyon, France. 14APHP, Department of Molecular Genetics, Pharmacogenetics and Hormonology, Bicêtre Paris-Sud Hospital, Le Kremlin-Bicetre, France. 15APHP, Hôpital Necker Enfants Malades,15APHP, Hôpital Necker Enfants Malades, INSERM U115115APHP, Hôpital Necker Enfants Malades, INSERM U1151 INSERM U1151, Paris, France
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